We report successful bone marrow transplantation in a child with a severe form of α-mannosidosis, type I. There was complete resolution of the recurrent sinopulmonary disease and organomegaly, improvement in the bony disease, and stabilization of neurocognitive function.
|Original language||English (US)|
|Number of pages||4|
|Journal||The Journal of Pediatrics|
|Publication status||Published - 1998|
ASJC Scopus subject areas
- Pediatrics, Perinatology, and Child Health